ea0070aep1064 | Hot topics (including COVID-19) | ECE2020
Csákváry Violetta
, Muzsnai Agota
, Raduk Dmitri
, Chaychenko Tetyana
, Bentz Damholt Birgitte
, Bakhtadze Bagci Ekaterine
, Teifel Michael
, Ammer Nicola
Growth hormone deficiency (GHD) in children is a rare, aetiologically diverse condition that results in growth failure and short stature. Inadequate response to two different growth hormone stimulation tests (GHST) is required for the diagnosis of GHD. Macimorelin acetate, a potent, orally administered growth hormone (GH) secretagogue, is approved by the FDA and EMA for the diagnosis of adult GHD. Study AEZS-130-P01 is the first of two studies to investigate macimorelin acetat...